Juvenile Neuronal Ceroid Lipofuscinosis (CLN3, Batten Disease)
Also known as: Juvenile Neuronal Ceroid Lipofuscinosis / Neuronal ceroid lipofuscinosis / Batten's syndrome / Batten's disease / Juvenile neuronal ceroid lipofuscinosis (disorder) / Vogt-Spielmeyer disease / Neuronal ceroid lipofuscinosis (disorder) / Neuronal ceroid lipofuscinosis NOS / Neuronal Ceroid-Lipofuscinoses
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB00688 | Mycophenolate mofetil | 2 | Completed | 1 |
DB01241 | Gemfibrozil | 3 | Not Yet Recruiting | 1 |