MPS VI (DBCOND0053627)

Identifiers

Synonyms
Not Available

Associated Data

Indicated Drugs and Targets
Not Available
Clinical Trials
IdentifierTitleDrug(s)PurposePhaseStatus
NCT01387854
Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02No drug interventionsNot AvailableNot Availablecompleted
NCT04532047
In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseasestreatment1recruiting
NCT01961518
Screening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy SyndromeNo drug interventionsNot AvailableNot Availablecompleted
NCT05845749
Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VIother1 / 2recruiting
NCT03632213
Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VItreatment2active_not_recruiting