Pegademase Completed Phase 3 Trials for ADA-SCID / Severe Combined Immunodeficiency Syndrome / Adenosine Deaminase Deficiency Treatment
Indications | Status | Purpose | Phase |
---|---|---|---|
Completed | Treatment | 3 |
clinicaltrials.gov Identifier | Title | Drugs |
---|---|---|
NCT01420627 | EZN-2279 in Patients With ADA-SCID |