Glycerol phenylbutyrate Completed Phase 3 Trials for deficiencies in enzymes of the urea cycle Treatment

IndicationsStatusPurposePhase
CompletedTreatment3
clinicaltrials.gov IdentifierTitleDrugs
NCT00947297Study of the Safety of HPN (Hyperion)-100 for the Long-Term Treatment of Urea Cycle Disorders (Treat UCD)
NCT00992459Efficacy and Safety of HPN-100 for the Treatment of Adults With Urea Cycle Disorders
NCT01347073Study of the Safety, Pharmacokinetics and Efficacy of HPN-100, in Pediatric Subjects With Urea Cycle Disorders (UCDs)