Vestronidase alfa Completed Phase 2 Trials for Mucopolysaccharidosis Type VII / Sly Syndrome / Mucopolysaccharidosis (MPS) Treatment
Indications | Status | Purpose | Phase |
---|---|---|---|
Completed | Treatment | 2 |
clinicaltrials.gov Identifier | Title | Drugs |
---|---|---|
NCT02418455 | Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age |