Vestronidase alfa Completed Phase 3 Trials for Mucopolysaccharidosis Type VII / Sly Syndrome / Mucopolysaccharidosis (MPS) Treatment

IndicationsStatusPurposePhase
CompletedTreatment3
clinicaltrials.gov IdentifierTitleDrugs
NCT02432144
A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7)