Risdiplam Completed Phase 2 Trials for Spinal Muscular Atrophy (SMA) Treatment
Indications | Status | Purpose | Phase |
---|---|---|---|
Completed | Treatment | 2 |
clinicaltrials.gov Identifier | Title | Drugs |
---|---|---|
NCT02908685 | A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants | |
NCT02913482 | Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy |