Risdiplam Recruiting Phase 4 Trials for Spinal Muscular Atrophy (SMA) Treatment
| Indications | Status | Purpose | Phase |
|---|---|---|---|
| Recruiting | Treatment | 4 |
| clinicaltrials.gov Identifier | Title | Drugs |
|---|---|---|
| NCT05861999 | A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy | |
| NCT05861986 | A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy | |
| NCT05232929 | Long-Term Follow-Up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA) |