Niemann-Pick Disease, Type C Active Not Recruiting Phase 2 Trials for AZ-3102 (DB18502)
Also known as: Niemann-Pick Type C Disease / Niemann-Pick Disease Type C / Niemann-Pick disease, type C (disorder)
| Indication | Status | Phase |
|---|---|---|
| DBCOND0001494 (Niemann-Pick Disease, Type C) | Active Not Recruiting | 2 |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT05758922 | Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease | Treatment |