Hemophilia B

Also known as: Christmas Disease / Haemophilia B / Hemophilia Bs / Bs, Hemophilia / Hereditary factor IX deficiency / Factor IX deficiency (disorder) / Factor IX deficiency / Congenital factor IX disorder / Hemophilia B (disorder) / Hemophilia B (Factor IX) / Haemophilia B (Factor IX) / Christmas disease (Factor IX)

DrugDrug NameDrug Description
DB13884Albutrepenonacog alfaA recombinant Factor IX fused to recombinant human albumin used to treat hemophilia B.
DB00100Coagulation Factor IX (Recombinant)A form of recombinant human coagulation Factor IX used to treat hemophilia B.
DB00036Coagulation factor VIIa Recombinant HumanA form of recombinant human coagulation Factor VII used to treat hemophilia A and B.
DB16791Etranacogene dezaparvovecAn adeno-associated virus vector-based gene therapy used for the treatment of hemophilia B (congenital factor IX deficiency).
DB11330Factor IX Complex (Human)A Factor IX complex used to prevent and treat bleeding episodes in hemophilia B or vitamin K antagonist therapy.
DrugDrug NamePhaseStatusCount
DB16788Adlinacogene civaparvovec1Terminated1
DB00062Albumin human1Completed1
DB17704BBM-H9011Recruiting1
DB16188Befovacimab1Completed1
DB00100Coagulation Factor IX (Recombinant)1Completed3
DB13152Coagulation Factor IX Human1Completed1
DB13150Coagulation factor VII human1Completed3
DB13150Coagulation factor VII human1Withdrawn1
DB00036Coagulation factor VIIa Recombinant Human1Completed1
DB00036Coagulation factor VIIa Recombinant Human1Withdrawn1
DB17707Dalcinonacog alfa1Completed1
DB11608Eftrenonacog alfa1Completed2
DB11661Eptacog alfa pegol (activated)1Completed2
DB16783Fidanacogene elaparvovec1Terminated1
DB15002Fitusiran1Completed1
DB17715MOD-50141Completed1
DB13933Nonacog beta pegol1Completed1
DB00062Albumin human1 / 2Completed1
DB13884Albutrepenonacog alfa1 / 2Completed1
DB17845BAX 3351 / 2Active Not Recruiting1
DB13152Coagulation Factor IX Human1 / 2Completed2
DB15002Fitusiran1 / 2Completed1
DB17698SerpinPC1 / 2Active Not Recruiting1
DB16805Verbrinacogene setparvovec1 / 2Terminated2
DB05016Ataluren2Terminated1
DB00100Coagulation Factor IX (Recombinant)2Completed1
DB13152Coagulation Factor IX Human2Completed2
DB00036Coagulation factor VIIa Recombinant Human2Completed1
DB00055Drotrecogin alfa2Recruiting2
DB16783Fidanacogene elaparvovec2Active Not Recruiting1
DB16783Fidanacogene elaparvovec2Completed1
DB17698SerpinPC2Recruiting2
DB12409Vatreptacog alfa2Completed1
DB00100Coagulation Factor IX (Recombinant)2 / 3Completed2
DB13201Trenonacog alfa2 / 3Completed1
DB13151Anti-inhibitor coagulant complex3Completed1
DB00100Coagulation Factor IX (Recombinant)3Completed8
DB00100Coagulation Factor IX (Recombinant)3Terminated1
DB13152Coagulation Factor IX Human3Active Not Recruiting1
DB13152Coagulation Factor IX Human3Completed8
DB13150Coagulation factor VII human3Recruiting1
DB00036Coagulation factor VIIa Recombinant Human3Completed1
DB11608Eftrenonacog alfa3Completed2
DB16783Fidanacogene elaparvovec3Active Not Recruiting1
DB15002Fitusiran3Completed2
DB02325Isopropyl alcohol3Completed5
DB17725Marstacimab3Active Not Recruiting1
DB17725Marstacimab3Recruiting2
DB13933Nonacog beta pegol3Active Not Recruiting1
DB13933Nonacog beta pegol3Completed5
DB13201Trenonacog alfa3Completed1
DB13201Trenonacog alfa3Terminated1
DB06298Trenonacog alfa3Withdrawn1
DB00100Coagulation Factor IX (Recombinant)4Completed4
DB13152Coagulation Factor IX Human4Completed4
DB16788Adlinacogene civaparvovecNot AvailableActive Not Recruiting1
DB00025Antihemophilic factor, human recombinantNot AvailableCompleted1
DB00025Antihemophilic factor, human recombinantNot AvailableTerminated1
DB00100Coagulation Factor IX (Recombinant)Not AvailableCompleted6
DB00100Coagulation Factor IX (Recombinant)Not AvailableTerminated1
DB13152Coagulation Factor IX HumanNot AvailableCompleted3
DB13152Coagulation Factor IX HumanNot AvailableEnrolling by Invitation1
DB13152Coagulation Factor IX HumanNot AvailableRecruiting1
DB13150Coagulation factor VII humanNot AvailableCompleted3
DB00036Coagulation factor VIIa Recombinant HumanNot AvailableCompleted1
DB12820ConcizumabNot AvailableEnrolling by Invitation1
DB16790Devafidugene civaparvovecNot AvailableActive Not Recruiting1
DB11607Efmoroctocog alfaNot AvailableCompleted1
DB11607Efmoroctocog alfaNot AvailableRecruiting1
DB11607Efmoroctocog alfaNot AvailableTerminated1
DB11608Eftrenonacog alfaNot AvailableActive Not Recruiting1
DB11608Eftrenonacog alfaNot AvailableCompleted2
DB11608Eftrenonacog alfaNot AvailableRecruiting1
DB11608Eftrenonacog alfaNot AvailableTerminated1
DB13933Nonacog beta pegolNot AvailableEnrolling by Invitation2
DB00935OxymetazolineNot AvailableRecruiting1
DB01022PhylloquinoneNot AvailableCompleted1
DB16789Tefidsogene civaparvovecNot AvailableActive Not Recruiting1