Mevalonate Kinase Deficiency

Also known as: Periodic fever syndromes / Deficiency of mevalonate kinase (disorder)

DrugDrug NameDrug Description
DB06168CanakinumabAn interleukin-1β blocker used to treat Periodic Fever Syndromes such as Cryopyrin-Associated Periodic Syndromes (CAPS) and Familial Mediterranean Fever (FMF), and also to treat active Systemic Juvenile Idiopathic Arthritis (SJIA).
DrugDrug NameTargetType
DB06168CanakinumabInterleukin-1 betatarget
DrugDrug NamePhaseStatusCount
DB06168Canakinumab2Completed1