Tuberous Sclerosis

Also known as: TSC / Tuberous Sclerosis Complex (TSC) / Tuberous Sclerosis Complex / Epiloya / Brain sclerosis / Tuberous sclerosis syndrome (disorder) / Epiloia

DrugDrug NameDrug Description
DB09061CannabidiolAn active cannabinoid used as an adjunctive treatment for the management of seizures associated with Lennox-Gastaut syndrome or Dravet syndrome and symptomatic relief of moderate to severe neuropathic pain or other painful conditions, like cancer.
DB00877SirolimusAn mTOR inhibitor immunosuppressant used to prevent organ transplant rejections, treat lymphangioleiomyomatosis, and treat adults with perivascular epithelioid cell tumors.
DrugDrug NameTargetType
DB09061CannabidiolCytochrome P450 2C9enzyme
DB09061CannabidiolCytochrome P450 2C19enzyme
DB09061CannabidiolCytochrome P450 2D6enzyme
DB09061CannabidiolCytochrome P450 3A4enzyme
DB09061CannabidiolCannabinoid receptor 1target
DB09061CannabidiolCannabinoid receptor 2target
DB09061CannabidiolG-protein coupled receptor 12target
DB09061CannabidiolGlycine receptor subunit alpha-1target
DB09061CannabidiolGlycine receptor (alpha-1/beta)target
DB09061CannabidiolGlycine receptor subunit alpha-3target
DB09061CannabidiolN-arachidonyl glycine receptortarget
DB09061CannabidiolG-protein coupled receptor 55target
DB09061Cannabidiol5-hydroxytryptamine receptor 1Atarget
DB09061Cannabidiol5-hydroxytryptamine receptor 2Atarget
DB09061CannabidiolNeuronal acetylcholine receptor subunit alpha-7target
DB09061CannabidiolDelta-type opioid receptortarget
DB09061CannabidiolMu-type opioid receptortarget
DB09061CannabidiolPeroxisome proliferator-activated receptor gammatarget
DB09061CannabidiolCytochrome P450 3A5enzyme
DB09061CannabidiolSerotonin N-acetyltransferaseenzyme
DB09061CannabidiolCytochrome P450 1A1enzyme
DB09061CannabidiolFatty-acid amide hydrolase 1enzyme
DB09061CannabidiolArachidonate 5-lipoxygenaseenzyme
DB09061CannabidiolArachidonate 15-lipoxygenaseenzyme
DB09061CannabidiolQuinone oxidoreductaseenzyme
DB09061CannabidiolMultidrug resistance-associated protein 1transporter
DB09061CannabidiolATP-binding cassette sub-family G member 2transporter
DB09061CannabidiolEquilibrative nucleoside transporter 1transporter
DB09061CannabidiolTransient receptor potential cation channel subfamily V member 1target
DB09061CannabidiolVoltage-dependent T-type calcium channel subunit alpha-1Gtarget
DB09061CannabidiolVoltage-dependent T-type calcium channel subunit alpha-1Htarget
DB09061CannabidiolVoltage-dependent T-type calcium channel subunit alpha-1Itarget
DB09061CannabidiolTransient receptor potential cation channel subfamily A member 1target
DB09061CannabidiolTransient receptor potential cation channel subfamily M member 8target
DB09061CannabidiolTransient receptor potential cation channel subfamily V member 2target
DB09061CannabidiolTransient receptor potential cation channel subfamily V member 3target
DB09061CannabidiolTransient receptor potential cation channel subfamily V member 4target
DB09061CannabidiolVoltage-dependent anion-selective channel protein 1target
DB09061Cannabidiol5-hydroxytryptamine receptor 3Atarget
DB09061CannabidiolAdenosine receptor A1target
DB09061CannabidiolProstaglandin G/H synthase 1target
DB09061CannabidiolProstaglandin G/H synthase 2target
DB09061CannabidiolAcetyl-CoA acetyltransferase, mitochondrialtarget
DB09061CannabidiolSteroid 17-alpha-hydroxylase/17,20 lyasetarget
DB09061Cannabidiol3-hydroxy-3-methylglutaryl-coenzyme A reductasetarget
DB09061CannabidiolGlutathione reductase, mitochondrialtarget
DB09061CannabidiolGlutathione peroxidase 1target
DB09061CannabidiolIndoleamine 2,3-dioxygenase 1target
DB09061CannabidiolCytochrome P450 1B1target
DB09061CannabidiolNAD(P)H dehydrogenase [quinone] 1target
DB09061CannabidiolCatalasetarget
DB09061CannabidiolCytochrome P450 3A5target
DB09061CannabidiolCytochrome P450 2D6target
DB09061CannabidiolSuperoxide dismutase [Cu-Zn]target
DB09061CannabidiolCytochrome P450 1A2target
DB09061CannabidiolCytochrome P450 3A7target
DB09061CannabidiolSerotonin N-acetyltransferasetarget
DB09061CannabidiolN-acylethanolamine-hydrolyzing acid amidasetarget
DB09061CannabidiolCytochrome P450 1A2enzyme
DB09061CannabidiolCytochrome P450 1B1enzyme
DB09061CannabidiolCytochrome P450 2A6enzyme
DB09061CannabidiolCytochrome P450 2B6enzyme
DB09061CannabidiolCytochrome P450 2C8enzyme
DB09061CannabidiolCytochrome P450 2E1enzyme
DB09061CannabidiolCytochrome P450 3A7enzyme
DB09061CannabidiolUDP-glucuronosyltransferase 1-7enzyme
DB09061CannabidiolUDP-glucuronosyltransferase 1-9enzyme
DB09061CannabidiolUDP-glucuronosyltransferase 2B7enzyme
DB09061CannabidiolUDP-glucuronosyltransferase 2B17enzyme
DB09061CannabidiolP-glycoprotein 1transporter
DB09061CannabidiolCytochrome P450 2J2enzyme
DB09061CannabidiolLiver carboxylesterase 1enzyme
DB00877SirolimusCytochrome P450 3A4enzyme
DB00877SirolimusSerine/threonine-protein kinase mTORtarget
DB00877SirolimusCytochrome P450 3A5enzyme
DB00877SirolimusCytochrome P450 3A7enzyme
DB00877SirolimusP-glycoprotein 1transporter
DB00877SirolimusSolute carrier organic anion transporter family member 1B1transporter
DB00877SirolimusMultidrug and toxin extrusion protein 1transporter
DB00877SirolimusSerum albumincarrier
DB00877SirolimusAlpha-1-acid glycoprotein 1carrier
DB00877SirolimusApolipoproteinscarrier
DrugDrug NamePhaseStatusCount
DB00877Sirolimus1Completed1
DB01590Everolimus1 / 2Completed5
DB00641Simvastatin1 / 2Completed1
DB00877Sirolimus1 / 2Completed2
DB00945Acetylsalicylic acid2Unknown Status1
DB01590Everolimus2Completed4
DB01590Everolimus2Unknown Status1
DB05087Ganaxolone2Completed1
DB00571Propranolol2Completed1
DB08839Serotonin2Not Yet Recruiting1
DB01104Sertraline2Not Yet Recruiting1
DB00877Sirolimus2Completed4
DB00877Sirolimus2Recruiting2
DB00877Sirolimus2Terminated1
DB00877Sirolimus2Unknown Status1
DB01080Vigabatrin2Completed1
DB01590Everolimus2 / 3Unknown Status1
DB00877Sirolimus2 / 3Completed1
DB00877Sirolimus2 / 3Recruiting1
DB01080Vigabatrin2 / 3Recruiting1
DB09061Cannabidiol3Completed2
DB01590Everolimus3Active Not Recruiting1
DB01590Everolimus3Completed2
DB05087Ganaxolone3Enrolling by Invitation1
DB09061Cannabidiol4Recruiting1
DB00254Doxycycline4Completed1