Myasthenic Syndromes, Congenital

Also known as: Congenital Myasthenic Syndrome / Congenital Myasthenia (CM) / Congenital Myasthenic Syndromes / Congenital Myasthenia / Congenital myasthenic syndrome (disorder)

DrugDrug NameDrug Description
DB00545PyridostigmineA cholinesterase inhibitor used for symptomatic treatment of myasthenia gravis and congenital myasthenic syndromes and to reverse neuromuscular blockade by nondepolarizing muscle relaxants.
DrugDrug NamePhaseStatusCount
DB01001Albuterol1Completed1
DB01364Ephedrine1 / 2Unknown Status1
DB11640Amifampridine3Completed1
DB11640AmifampridineNot AvailableApproved for Marketing1
DB11640AmifampridineNot AvailableNo Longer Available4