Mucopolysaccharidosis VII Recruiting Phase 1 Trials for Laronidase (DB00090)

Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis Type 7 / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

IndicationStatusPhase
DBCOND0002603 (Mucopolysaccharidosis VII)Recruiting1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT04532047
In Utero Enzyme Replacement Therapy for Lysosomal Storage DiseasesTreatment