Mucopolysaccharidosis VII Recruiting Phase 1 Trials for Laronidase (DB00090)
Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis Type 7 / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome
Indication | Status | Phase |
---|---|---|
DBCOND0002603 (Mucopolysaccharidosis VII) | Recruiting | 1 |
clinicaltrials.gov Identifier | Title | Purpose | Drugs |
---|---|---|---|
NCT04532047 | In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases | Treatment |