Mucopolysaccharidosis VII Recruiting Phase 1 Trials for Alglucosidase alfa (DB01272)
Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis Type 7 / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome
| Indication | Status | Phase |
|---|---|---|
| DBCOND0002603 (Mucopolysaccharidosis VII) | Recruiting | 1 |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT04532047 | In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases | Treatment |