Mucopolysaccharidosis VII Completed Phase 1 / 2 Trials for Vestronidase alfa (DB12366)

Back to Mucopolysaccharidosis VII

Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis Type 7 / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

Indication	Status	Phase
DBCOND0002603 (Mucopolysaccharidosis VII)	Completed	1 / 2

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT01856218	An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Beta-glucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)	Treatment	Vestronidase alfa (DB12366)