Mucopolysaccharidosis VII Completed Phase 2 Trials for Vestronidase alfa (DB12366)

Back to Mucopolysaccharidosis VII

Also known as: MPS VII / Mucopolysaccharidosis Type VII / Mucopolysaccharidosis Type 7 / Other mucopolysaccharidoses / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

Indication	Status	Phase
DBCOND0002603 (Mucopolysaccharidosis VII)	Completed	2

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT02418455	Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age	Treatment	Vestronidase alfa (DB12366)