Gangliosidosis, GM1 Completed Phase 2 Trials for Clofarabine (DB00631)

Also known as: GM1 Gangliosidosis / [X]Other gangliosidosis (disorder) / GM1 gangliosidosis (disorder) / GM>1< gangliosidosis (disorder) / Deficiency of beta-galactosidase (disorder) / Mucopolysaccharidosis type IVB (disorder) / Mucopolysaccharidosis, MPS-IV-B (disorder) [Ambiguous] / Beta-Galactosidase Deficiency

IndicationStatusPhase
DBCOND0003891 (Gangliosidosis, GM1)Completed2
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT00383448HSCT for High Risk Inherited Inborn ErrorsTreatment