Sucrase-isomaltase deficiency

Also known as: Sucrase Isomaltase Deficiency / Deficiency of isomaltase (disorder) / Sucrase-isomaltase deficiency (disorder) / Deficiency of beta-fructofuranosidase (disorder)

DrugDrug NameDrug Description
DB06760SacrosidaseAn enzyme replacement therapy used for the treatment of congenital sucrase-isomaltase deficiency (CSID).
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB06760Sacrosidase4Recruiting1