Beta-Thalassemia Recruiting Phase 3 Trials for Exagamglogene autotemcel (DB15572)

Also known as: Β -Thalassemia / Β Thalassemia / Thalassemia, Beta / B-Thalassemia / Β-thalassemia / Thalassaemia beta / Beta Thalassaemia / Beta Thalassemia / B Thalassemia / Thalassemia beta / Beta thalassemia (disorder) / Beta-thalassaemia / Thalassaemia intermedia / Thalassemia intermedia (disorder) / Thalassemia intermedia / Mediterranean anemia / Mediterranean anaemia / Thalassemia major / Cooley's anaemia / Thalassaemia major / Thalassemia major (disorder) / Homozygous beta thalassemia (disorder) / Cooley's anemia

IndicationStatusPhase
DBCOND0027982 (Beta-Thalassemia)Recruiting3
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT05356195Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)Treatment
NCT05477563Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell DiseaseTreatment