Inborn Errors of Metabolism
Also known as: Inborn error of metabolism / Metabolism, Inborn Errors / Inborn error of metabolism NOS / Inborn error of metabolism (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB00087 | Alemtuzumab | 1 | Completed | 1 |
DB01073 | Fludarabine | 1 | Completed | 1 |
DB01005 | Hydroxyurea | 1 | Completed | 1 |
DB01042 | Melphalan | 1 | Completed | 1 |
DB04572 | Thiotepa | 1 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 1 |
DB09312 | Antilymphocyte immunoglobulin (horse) | 2 | Completed | 1 |
DB01008 | Busulfan | 2 | Completed | 2 |
DB06775 | Carglumic acid | 2 | Withdrawn | 1 |
DB00531 | Cyclophosphamide | 2 | Completed | 1 |
DB01073 | Fludarabine | 2 | Completed | 1 |
DB01042 | Melphalan | 2 | Completed | 1 |
DB17950 | OT-15 | 2 | Withdrawn | 1 |
DB04951 | Pirfenidone | 2 | Completed | 1 |
DB04572 | Thiotepa | 2 | Completed | 1 |
DB11678 | Treosulfan | 2 | Completed | 1 |
DB06775 | Carglumic acid | 2 / 3 | Unknown Status | 1 |
DB04974 | Rimiducid | Not Available | No Longer Available | 1 |