Inborn Errors of Metabolism

Also known as: Inborn error of metabolism / Metabolism, Inborn Errors / Inborn error of metabolism NOS / Inborn error of metabolism (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab1Completed1
DB01073Fludarabine1Completed1
DB01005Hydroxyurea1Completed1
DB01042Melphalan1Completed1
DB04572Thiotepa1Completed1
DB00087Alemtuzumab2Completed1
DB09312Antilymphocyte immunoglobulin (horse)2Completed1
DB01008Busulfan2Completed2
DB06775Carglumic acid2Withdrawn1
DB00531Cyclophosphamide2Completed1
DB01073Fludarabine2Completed1
DB01042Melphalan2Completed1
DB17950OT-152Withdrawn1
DB04951Pirfenidone2Completed1
DB04572Thiotepa2Completed1
DB11678Treosulfan2Completed1
DB06775Carglumic acid2 / 3Unknown Status1
DB04974RimiducidNot AvailableNo Longer Available1