Lysosomal Storage Diseases
Also known as: Lysosomal Disease / Lysosomal Storage Disorders / Lysosomal Diseases / Lysosomal Storage Disease / Lysosomal Storage Disorder / Disorder of lysosomal enzyme (disorder)
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB00087 | Alemtuzumab | 1 | Completed | 1 |
DB01073 | Fludarabine | 1 | Completed | 1 |
DB01005 | Hydroxyurea | 1 | Completed | 1 |
DB00090 | Laronidase | 1 | Terminated | 2 |
DB01042 | Melphalan | 1 | Completed | 1 |
DB04572 | Thiotepa | 1 | Completed | 1 |
DB16804 | Bomtabegagene bavoparvovec | 1 / 2 | Recruiting | 1 |
DB00959 | Methylprednisolone | 1 / 2 | Recruiting | 1 |
DB00635 | Prednisone | 1 / 2 | Recruiting | 1 |
DB00073 | Rituximab | 1 / 2 | Recruiting | 1 |
DB00877 | Sirolimus | 1 / 2 | Recruiting | 1 |
DB00087 | Alemtuzumab | Not Available | Completed | 1 |
DB00631 | Clofarabine | Not Available | Completed | 1 |
DB06189 | Clofarabine | Not Available | Completed | 1 |
DB00091 | Cyclosporine | Not Available | Completed | 1 |
DB00090 | Laronidase | Not Available | Completed | 1 |
DB01042 | Melphalan | Not Available | Completed | 1 |
DB00688 | Mycophenolate mofetil | Not Available | Completed | 1 |
DB04974 | Rimiducid | Not Available | No Longer Available | 1 |