Genetic Diseases, Inborn

Also known as: Genetic Disease, Inborn / Inborn Genetic Diseases

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00741Hydrocortisone1Completed1
DB18620AOC 10012Active Not Recruiting1
DB15744Allogeneic Cardiosphere-Derived Cells2Completed1
DB12023Benralizumab2Completed1
DB05528Mipomersen2Completed2
DB15572Exagamglogene autotemcel2 / 3Active Not Recruiting1
DB14973Abrocitinib3Completed2
DB15744Allogeneic Cardiosphere-Derived Cells3Recruiting1
DB05016Ataluren3Completed2
DB05016Ataluren3Terminated1
DB12159Dupilumab3Completed1
DB15572Exagamglogene autotemcel3Enrolling by Invitation1
DB15572Exagamglogene autotemcel3Recruiting2
DB05528Mipomersen3Completed2
DB14890Obicetrapib3Active Not Recruiting1
DB06372Rilonacept3Completed1
DB01018Guanfacine4Recruiting1
DB01076AtorvastatinNot AvailableCompleted1
DB01039FenofibrateNot AvailableCompleted1
DB00627NiacinNot AvailableCompleted1