Sandhoffs Disease
Also known as: Sandhoff Disease / Sandhoff disease (disorder) / GM2 gangliosidosis / GM2 gangliosidosis, unspecified / GM2 gangliosidosis (disorder) / Gangliosidoses, GM2
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB16803 | Cobnabexagene anvuparvovec | 1 | Active Not Recruiting | 1 |
DB00650 | Leucovorin | 1 / 2 | Completed | 1 |
DB00205 | Pyrimethamine | 1 / 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 1 |
DB00631 | Clofarabine | 2 | Completed | 1 |
DB06189 | Clofarabine | 2 | Completed | 1 |
DB01005 | Hydroxyurea | 2 | Completed | 1 |
DB16956 | L-Acetylleucine | 2 | Completed | 1 |
DB01042 | Melphalan | 2 | Completed | 1 |
DB13201 | Trenonacog alfa | 2 | Completed | 1 |
DB01008 | Busulfan | 2 / 3 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |
DB00419 | Miglustat | 3 | Completed | 1 |
DB14966 | Venglustat | 3 | Active Not Recruiting | 1 |
DB00419 | Miglustat | 4 | Terminated | 1 |