Spinal Muscular Atrophy Type III
Also known as: Muscular Atrophy, Spinal, Type III / Kugelberg-Welander disease / Kugelberg-Welander disease (disorder) / Juvenile Spinal Muscular Atrophy / Spinal muscular atrophy, unspecified / Muscular Atrophy, Spinal / Spinal amyotrophy / Spinal muscular atrophy (disorder) / Spinal muscular atrophy
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB06819 | Phenylbutyric acid | 1 / 2 | Terminated | 1 |
| DB02325 | Isopropyl alcohol | 3 | Active Not Recruiting | 1 |
| DB15528 | Onasemnogene abeparvovec | 3 | Active Not Recruiting | 1 |