Acid Maltase Deficiency (AMD) Completed Phase 1 Trials for Avalglucosidase alfa (DB16099)
Also known as: Acid Maltase Deficiency
Indication | Status | Phase |
---|---|---|
DBCOND0036876 (Acid Maltase Deficiency (AMD)) | Completed | 1 |
clinicaltrials.gov Identifier | Title | Purpose | Drugs |
---|---|---|---|
NCT01898364 | Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients. | Treatment |