Acid Maltase Deficiency (AMD) Completed Phase 1 Trials for Avalglucosidase alfa (DB16099)

Also known as: Acid Maltase Deficiency

IndicationStatusPhase
DBCOND0036876 (Acid Maltase Deficiency (AMD))Completed1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT01898364Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.Treatment