Sly Syndrome
Also known as: Other mucopolysaccharidoses / Mucopolysaccharidosis VII / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00087 | Alemtuzumab | 2 | Completed | 1 |
| DB00087 | Alemtuzumab | 2 | Terminated | 1 |
| DB01008 | Busulfan | 2 | Completed | 1 |
| DB01008 | Busulfan | 2 | Terminated | 1 |
| DB00531 | Cyclophosphamide | 2 | Completed | 1 |
| DB00531 | Cyclophosphamide | 2 | Terminated | 1 |
| DB00091 | Cyclosporine | 2 | Completed | 1 |
| DB00688 | Mycophenolate mofetil | 2 | Completed | 1 |
| DB12366 | Vestronidase alfa | 2 | Completed | 1 |
| DB12366 | Vestronidase alfa | 3 | Completed | 2 |
| DB12366 | Vestronidase alfa | Not Available | Available | 1 |