Sly Syndrome Terminated Phase 2 Trials for Alemtuzumab (DB00087)

Also known as: Other mucopolysaccharidoses / Mucopolysaccharidosis VII / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

IndicationStatusPhase
DBCOND0040268 (Sly Syndrome)Terminated2
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT00668564
Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of MetabolismTreatment