Sly Syndrome Completed Phase 2 Trials for Busulfan (DB01008)

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Also known as: Other mucopolysaccharidoses / Mucopolysaccharidosis VII / Mucopolysaccharidosis, MPS-VII (disorder) / Deficiency of beta-glucuronidase (disorder) / Sly's syndrome

Indication	Status	Phase
DBCOND0040268 (Sly Syndrome)	Completed	2

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT01043640	Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders	Treatment	Alemtuzumab (DB00087) Busulfan (DB01008) Cyclophosphamide (DB00531) Cyclosporine (DB00091) Mycophenolate mofetil (DB00688)