Wolman's Disease Completed Phase 2 / 3 Trials for Busulfan (DB01008)
Also known as: Wolman Disease / Other lipid storage disorders / Wolman's disease (disorder) / Lysosomal acid lipase deficiency / Lysosomal acid lipase deficiency (disorder)
| Indication | Status | Phase |
|---|---|---|
| DBCOND0040271 (Wolman's Disease) | Completed | 2 / 3 |
| clinicaltrials.gov Identifier | Title | Purpose | Drugs |
|---|---|---|---|
| NCT00176904 | Stem Cell Transplant for Inborn Errors of Metabolism | Treatment |