Wolman's Disease Terminated Phase 2 Trials for Busulfan (DB01008)

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Also known as: Wolman Disease / Other lipid storage disorders / Wolman's disease (disorder) / Lysosomal acid lipase deficiency / Lysosomal acid lipase deficiency (disorder)

Indication	Status	Phase
DBCOND0040271 (Wolman's Disease)	Terminated	2

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT00668564	Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism	Treatment	Alemtuzumab (DB00087) Busulfan (DB01008) Cyclophosphamide (DB00531)