Wolman's Disease Recruiting Phase 1 Trials for Idursulfase (DB01271)

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Also known as: Wolman Disease / Other lipid storage disorders / Wolman's disease (disorder) / Lysosomal acid lipase deficiency / Lysosomal acid lipase deficiency (disorder)

Indication	Status	Phase
DBCOND0040271 (Wolman's Disease)	Recruiting	1

clinicaltrials.gov Identifier	Title	Purpose	Drugs
NCT04532047	In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases	Treatment	Alglucosidase alfa (DB01272) Elosulfase alfa (DB09051) Galsulfase (DB01279) Idursulfase (DB01271) Laronidase (DB00090) Sebelipase alfa (DB11563) Vestronidase alfa (DB12366)