Wolman's Disease Recruiting Phase 1 Trials for Sebelipase alfa (DB11563)

Also known as: Wolman Disease / Other lipid storage disorders / Wolman's disease (disorder) / Lysosomal acid lipase deficiency / Lysosomal acid lipase deficiency (disorder)

IndicationStatusPhase
DBCOND0040271 (Wolman's Disease)Recruiting1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT04532047
In Utero Enzyme Replacement Therapy for Lysosomal Storage DiseasesTreatment