Glycogen Storage Disease Type II (GSD II) Completed Phase 2 Trials for Alglucosidase alfa (DB01272)
Also known as: Glycogen Storage Disease Type II GSD II / Glycogen Storage Disease Type II (GSD-II)
Indication | Status | Phase |
---|---|---|
DBCOND0041318 (Glycogen Storage Disease Type II (GSD II)) | Completed | 2 |
clinicaltrials.gov Identifier | Title | Purpose | Drugs |
---|---|---|---|
NCT00765414 | Extension Study of Long-term Safety and Efficacy of Myozyme for a Single Patient With Pompe Disease Who Were Previously Enrolled in Genzyme Sponsored ERT Studies. | Treatment | |
NCT00250939 | A Study of rhGAA in Patients With Late-Onset Pompe Disease | Treatment |