Glycogen Storage Disease Type II (GSD II) Completed Phase 1 Trials for Avalglucosidase alfa (DB16099)

Also known as: Glycogen Storage Disease Type II GSD II / Glycogen Storage Disease Type II (GSD-II)

IndicationStatusPhase
DBCOND0041318 (Glycogen Storage Disease Type II (GSD II))Completed1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT01898364Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.Treatment