Pompe's Disease
Also known as: Pompe Disease / Cardiac glycogenosis / Acid maltase deficiency / Glycogen storage disease type II / Type II glycogen storage disease
Drug | Drug Name | Drug Description |
---|---|---|
DB01272 | Alglucosidase alfa | An acid alpha- glucosidase (GAA) derivative used as an enzyme replacement therapy for the treatment of Pompe disease in infants and pediatric patients caused by GAA deficiency. |
DB16099 | Avalglucosidase alfa | A lysosomal glycogen-specific enzyme that is used to treat patients one year of age and older with late-onset Pompe disease, or lysosomal acid alpha-glucosidase (GAA) deficiency. |