Hurlers Syndrome Completed Phase 1 Trials for Abatacept (DB01281)

Also known as: Hurler's Syndrome / Hurler Syndrome / Dysostosis multiplex (disorder) / Mucopolysaccharidosis, MPS-I (disorder) / MPS I H / (Mucopolysaccharidosis: (& [gargoylism]/[Hunter][Hurler]/[lipochondrodyst]/[Maroteaux-Lamy]/[Morquio-Brailsford]/[osteochondrodystrophy]/[Sanfilippo]/[Scheie]) or (dysostos multi) / Mucopolysaccharidosis, MPS-I-H (disorder) / Hurler's disease / Mucopolysaccharidosis, type 1: (& [gargoylism] or [Hurler's syndrome] or [Scheie's syndrome]) / Mucopolysaccharidosis I / Mucopolysaccharidosis type I [Ambiguous] / Mucopolysaccharidosis, type I

IndicationStatusPhase
DBCOND0043682 (Hurlers Syndrome)Completed1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT01917708Bone Marrow Transplant With Abatacept for Non-Malignant DiseasesSupportive Care