Friedreich's Ataxia

Also known as: Friedreich Ataxia / Friedreich ataxia (disorder)

DrugDrug NameDrug Description
DB12513OmaveloxoloneA semisynthetic triterpenoid used to treat Friedreich’s ataxia in adults and adolescents 16 years and older.
DrugDrug NamePhaseStatusCount
DB00959Methylprednisolone0Completed1
DB01098Rosuvastatin0Completed1
DB17010CTI-16011Completed2
DB09081Idebenone1Completed2
DB02758Indolepropionic acid1Completed1
DB12513Omaveloxolone1Not Yet Recruiting1
DB00635Prednisone1Recruiting1
DB09274Artesunate1 / 2Recruiting1
DB08826Deferiprone1 / 2Completed1
DB11981Elamipretide1 / 2Active Not Recruiting1
DB01592Iron1 / 2Completed1
DB02709Resveratrol1 / 2Completed1
DB17010CTI-16012Completed1
DB08826Deferiprone2Completed1
DB00016Erythropoietin2Completed2
DB06414Etravirine2Completed1
DB01381Ginkgo biloba2Completed1
DB09081Idebenone2Completed1
DB00033Interferon gamma-1b2Completed1
DB15021Leriglitazone2Completed1
DB16067Luvadaxistat2Completed1
DB02701Nicotinamide2Withdrawn1
DB12513Omaveloxolone2Active Not Recruiting1
DB02709Resveratrol2Active Not Recruiting1
DB14094Tocopherylquinone2Completed1
DB11917Vatiquinone2Active Not Recruiting1
DB11917Vatiquinone2Completed2
DB01273Varenicline2 / 3Terminated1
DB11917Vatiquinone2 / 3Completed1
DB09081Idebenone3Completed5
DB00033Interferon gamma-1b3Completed3
DB01132Pioglitazone3Completed1
DB11917Vatiquinone3Enrolling by Invitation1
DB01156Bupropion4Completed1
DB00136Calcitriol4Completed1
DB00215Citalopram4Completed1
DB08842AcetylcarnitineNot AvailableUnknown Status1