Gangliosidoses, GM2
Also known as: GM2 Gangliosidoses / Gangliosidoses GM2 / GM2-Gangliosidosis / GM2 Gangliosidosis / GM2 gangliosidosis, unspecified / GM2 gangliosidosis (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00650 | Leucovorin | 1 / 2 | Completed | 1 |
| DB00205 | Pyrimethamine | 1 / 2 | Completed | 1 |
| DB18502 | AZ-3102 | 2 | Active Not Recruiting | 1 |
| DB16956 | L-Acetylleucine | 2 | Completed | 1 |
| DB00419 | Miglustat | 2 | Completed | 1 |
| DB13201 | Trenonacog alfa | 2 | Completed | 1 |
| DB00419 | Miglustat | 3 | Completed | 1 |
| DB00419 | Miglustat | 3 | Recruiting | 1 |
| DB00419 | Miglustat | 4 | Terminated | 1 |