Lysosomal Acid Lipase Deficiency
Also known as: Acid Lipase Deficiency / Lysosomal acid lipase deficiency (disorder) / Other lipid storage disorders / Wolman's disease / Wolman Disease / Wolman's disease (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB11563 | Sebelipase alfa | A recombinant lysosomal acid lipase used to treat lysosomal acid lipase deficiency. |
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB11563 | Sebelipase alfa | 1 / 2 | Completed | 1 |
| DB11563 | Sebelipase alfa | 2 | Completed | 2 |
| DB11563 | Sebelipase alfa | 2 | Terminated | 1 |
| DB11563 | Sebelipase alfa | 2 / 3 | Completed | 1 |
| DB11563 | Sebelipase alfa | 2 / 3 | Terminated | 1 |
| DB11563 | Sebelipase alfa | 3 | Completed | 1 |
| DB13147 | Pancrelipase lipase | Not Available | No Longer Available | 1 |
| DB11563 | Sebelipase alfa | Not Available | No Longer Available | 1 |