Hyperphenylalaninemia

Also known as: Hyperphenylalaninaemia / Hyperphenylalaninemia (disorder)

DrugDrug NameDrug Description
DB00360SapropterinA cofactor used as an adjunct to phenylalanine restriction in the treatment of phenylketonuria (PKU).
DrugDrug NamePhaseStatusCount
DB16326Sepiapterin1 / 2Completed1
DB00360SapropterinNot AvailableCompleted1
DB00360SapropterinNot AvailableTerminated1