Niemann-Pick Disease, Type C1
Also known as: Niemann-Pick Disease Type C1
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB14509 | Lithium carbonate | 0 | Unknown Status | 1 |
DB15146 | Adrabetadex | 1 | Completed | 1 |
DB15379 | Hydroxypropyl betadex | 1 | Completed | 1 |
DB15146 | Adrabetadex | 1 / 2 | Terminated | 1 |