Cholesterol Ester Storage Disease (CESD)
Also known as: Cholesterol Ester Storage Disease(CESD) / Cholesterol Ester Storage Disease / Cholesteryl ester storage disease / Cholesterol ester storage disease (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB11563 | Sebelipase alfa | 1 / 2 | Completed | 1 |
DB11563 | Sebelipase alfa | 2 | Completed | 1 |