Distal Myopathy With Rimmed Vacuoles (DMRV)

Also known as: Distal Myopathy With Rimmed Vacuoles / GNE myopathy / Inclusion body myopathy 2 (disorder) / Hereditary inclusion body myopathy

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB11797Aceneuramic acid2Terminated1
DB11797Aceneuramic acid3Completed2
DB11797Aceneuramic acid3Terminated1