Spinal Muscular Atrophy 1 Completed Phase 1 Trials for Onasemnogene abeparvovec (DB15528)

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IndicationStatusPhase
DBCOND0064014 (Spinal Muscular Atrophy 1)Completed1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT02122952Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1Treatment