Spinal Muscular Atrophy 1 Completed Phase 1 Trials for Onasemnogene abeparvovec (DB15528)

IndicationStatusPhase
DBCOND0064014 (Spinal Muscular Atrophy 1)Completed1
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT02122952Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1Treatment