Severe Haemophilia A
Also known as: Hemophilia A, Severe / Severe Hemophilia A / Severe hemophilia A (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB15561 | Valoctocogene roxaparvovec | An adeno-associated virus serotype 5 (AAV5)-based gene therapy containing a coagulation factor VIII complementary DNA used to treat severe hemophilia A. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB15561 | Valoctocogene roxaparvovec | Coagulation factor VIII (F8) | target |