Jansky-Bielschowsky Disease

Also known as: Neuronal ceroid lipofuscinosis / Late-Infantile Neuronal Ceroid Lipofuscinosis / Late-infantile neuronal ceroid lipofuscinosis (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB13173Cerliponase alfa1 / 2Completed2
DB13173Cerliponase alfa2Completed1