Jansky-Bielschowsky Disease
Also known as: Neuronal ceroid lipofuscinosis / Late-Infantile Neuronal Ceroid Lipofuscinosis / Late-infantile neuronal ceroid lipofuscinosis (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB13173 | Cerliponase alfa | 1 / 2 | Completed | 2 |
DB13173 | Cerliponase alfa | 2 | Completed | 1 |