Sphingomyelin Lipidosis
Also known as: Niemann-Pick Disease / Niemann-Pick Diseases / Niemann Pick Diseases / Niemann Pick Disease / Niemann-Pick disease, unspecified / Sphingomyelin/cholesterol lipidosis (disorder) / Acid Sphingomyelinase-deficient Niemann-Pick Disease / Acid sphingomyelinase deficiency / Niemann-Pick disease type A / Niemann-Pick disease, type A (disorder) / Niemann-Pick Disease, Type A
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB00419 | Miglustat | 1 | Completed | 1 |
DB12835 | Olipudase alfa | 1 / 2 | Completed | 1 |
DB02546 | Vorinostat | 1 / 2 | Completed | 1 |
DB12835 | Olipudase alfa | 2 | Completed | 1 |
DB01008 | Busulfan | 2 / 3 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |
DB12835 | Olipudase alfa | 2 / 3 | Completed | 1 |
DB12835 | Olipudase alfa | Not Available | Approved for Marketing | 1 |
DB12835 | Olipudase alfa | Not Available | Recruiting | 1 |