Sphingomyelin Lipidosis

Also known as: Niemann-Pick Disease / Niemann-Pick Diseases / Niemann Pick Diseases / Niemann Pick Disease / Niemann-Pick disease, unspecified / Sphingomyelin/cholesterol lipidosis (disorder) / Acid Sphingomyelinase-deficient Niemann-Pick Disease / Acid sphingomyelinase deficiency / Niemann-Pick disease type A / Niemann-Pick disease, type A (disorder) / Niemann-Pick Disease, Type A

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00419Miglustat1Completed1
DB12835Olipudase alfa1 / 2Completed1
DB02546Vorinostat1 / 2Completed1
DB12835Olipudase alfa2Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1
DB12835Olipudase alfa2 / 3Completed1
DB12835Olipudase alfaNot AvailableApproved for Marketing1
DB12835Olipudase alfaNot AvailableRecruiting1