Carnitine-acylcarnitine Translocase (CACT) Deficiency

Also known as: Carnitine-acylcarnitine translocase deficiency / Carnitine Acylcarnitine Translocase Deficiency / Carnitine acylcarnitine translocase deficiency (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB11677Triheptanoin2Completed1