Carnitine-acylcarnitine Translocase (CACT) Deficiency
Also known as: Carnitine-acylcarnitine translocase deficiency / Carnitine Acylcarnitine Translocase Deficiency / Carnitine acylcarnitine translocase deficiency (disorder)
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB11677 | Triheptanoin | 2 | Completed | 1 |