Mucopolysaccharidosis IIIB Completed Phase 1 / 2 Trials for Benzalkonium (DB11105)
Also known as: MPS 3 B / MPS IIIB (Sanfilippo Syndrome) / Sanfilippo B / Mucopolysaccharidosis III-B / Sanfilippo Syndrome B / Mucopolysaccharidosis Type 3 B / Sanfilippo Syndrome Type B / MPS III B / Mucopolysaccharidosis III, Type B (MPS IIIB) / Mucopolysaccharidosis Type IIIB / MPS IIIB (Sanfilippo B Syndrome) / Sanfilippo mucopolysaccharidoses / Mucopolysaccharidosis, MPS-III-B (disorder)
Indication | Status | Phase |
---|---|---|
DBCOND0074556 (Mucopolysaccharidosis IIIB) | Completed | 1 / 2 |
clinicaltrials.gov Identifier | Title | Purpose | Drugs |
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NCT02324049 | Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB) | Treatment |